How Each MPS Subtype Changes the Approach to Therapy

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2025-08-27 07:55:55 - Translate -

Mucopolysaccharidosis (MPS) represents a group of rare, genetic lysosomal storage conditions caused by specific enzyme deficiencies that impair glycosaminoglycan (GAG) breakdown. GAG accumulation results in progressive organ, bone, and tissue damage. Growing awareness of mucopolysaccharidosis causes is fueling sustained research initiatives and therapeutic development efforts. MPS Disease...

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